BioMarin focusses on developing first-in-class and best-in-class therapeutics that provide meaningful advances to patients who live with serious and life-threatening rare genetic diseases. BioMarin remains steadfast to its original mission to bring new treatments to market that will make a big impact on small patient populations.
BioMarin has a dedicated and professional approach to researching and understanding the potential of gene therapy. For any questions contact BioMarin Medical Information at medinfo@bmrn.com or click here.